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GLPG2451
GLPG2451 是一种囊性纤维化跨膜电导调节器 (CFTR) 的增强剂,有效增强低温挽救的 F508del CFTR,EC50 为 11.1 nM。
DNA31
DNA31 是囊性纤维化跨膜传导调节因子 (CFTR) 基因的全球最常见的 31 种突变。DNA31 用于针对囊性纤维化 (CF) 的新生儿筛查方案的第一级遗传测试。
CFTR corrector 1
An F508del-CFTR corrector and potentiator
PTI-428
Nesolicaftor (PTI-428) is a specific cystic fibrosis transmembrane conductance regulator (CFTR) amplifier that increases CFTR expression.
CFTR corrector 2
FDL169 is a CFTR corrector that is designed to fix and restore the function of the defective CFTR protein.
(R)-BPO-27
(R)-BPO-27是有效的CFTR抑制剂,IC50值为4nM。
BPO-27 racemate
BPO-27racemate是有效的CFTR抑制剂,IC50值为8nM。
GLPG1837(ABBV-974)
A CFTR potentiator
GlyH-101
A reversible CFTR channel blocker
PPQ-102
A CFTR channel inhibitor
VX-809
A F508del-CFTR corrector
VX-661
An investigational compound that promotes the maturation of delta F508 CFTR
CFTRinh-172
A potent CFTR channel blocker
Ivacaftor hydrate
Ivacaftor benzenesulfonate